Epidermolysis Bullosa News Home
WEBBecoming educated and informed about epidermolysis bullosa is a good first step. Here you’ll find general information about the disease, including diagnosis, symptoms, and causes. Get informed
Gene therapy gel heals decades-old wounds in trial for blistering …
WEBDec 15, 2022 · Stanford researchers have been working on gene therapies for epidermolysis bullosa, or “butterfly disease,” for over a decade. A new gel helped wounds heal and stay healed in a clinical trial.
FDA Approves First Topical Gene Therapy for Treatment of …
WEBMay 19, 2023 · FDA approves Vyjuvek, a herpes-simplex virus type 1 vector-based gene therapy, for the treatment of wounds in patients 6 months of age and older with dystrophic epidermolysis bullosa with...
Gene-therapy gel shows promise for blistering skin disease in …
WEBMar 28, 2022 · A gene therapy gel applied to the wounds of nine people — three of whom were children — with the blistering skin disease epidermolysis bullosa helped the wounds heal and remain healed for several months in a trial …
FDA approves first therapy for devastating skin condition
WEBMay 19, 2023 · The therapy, known as Vyjuvek and made by Krystal Biotech, will soon be available for patients with dystrophic epidermolysis bullosa, a genetic disease that causes painful blisters and...
A boy with a rare disease gets new skin, thanks to gene ... - AAAS
WEBNov 8, 2017 · The treatment—a whole-body graft of genetically modified stem cells—is the most ambitious attempt yet to treat a severe form of epidermolysis bullosa (EB), an often-fatal group of conditions that cause skin to blister and tear off at the slightest touch.
Trial of Beremagene Geperpavec (B-VEC) for Dystrophic Epidermolysis Bullosa
WEBDec 14, 2022 · We conducted a phase 3, double-blind, intrapatient randomized, placebo-controlled trial involving patients 6 months of age or older with genetically confirmed dystrophic epidermolysis bullosa....
First ever gene therapy gel corrects epidermolysis bullosa skin ...
WEBMar 28, 2022 · People with recessive dystrophic epidermolysis bullosa, a genetic condition that causes widespread skin blistering, have been successfully treated by inserting new collagen genes into their...
Topical Gene Therapy for Epidermolysis Bullosa | NEJM
WEBDec 14, 2022 · A new trial of gene therapy for dystrophic epidermolysis bullosa is notable for its context: the treatment of a skin disorder through topical application. This article describes the science...
Epidermolysis bullosa could soon get new kind of gene therapy
WEBApr 3, 2023 · A devastating skin condition could soon get its first medication, as the frontiers of gene therapy expand. Aaron Owens, who has a painful genetic skin blistering condition called epidermolysis ...